Serveur d'exploration sur les relations entre la France et l'Australie

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Consensus statement on definitions of disease, end points, and therapeutic response for pemphigus

Identifieur interne : 008E16 ( Main/Exploration ); précédent : 008E15; suivant : 008E17

Consensus statement on definitions of disease, end points, and therapeutic response for pemphigus

Auteurs : Dedee F. Murrell [Australie] ; Sarah Dick [États-Unis] ; A. R. Ahmed [États-Unis] ; Masayuki Amagai [Japon] ; Maria A. Barnadas [Espagne] ; Luca Borradori [Suisse] ; Jean-Claude Bystryn [États-Unis] ; Giuseppe Cianchini [Italie] ; Luis Diaz [États-Unis] ; David Fivenson [États-Unis] ; Russell Hall [États-Unis] ; Karen E. Harman [Royaume-Uni] ; Takashi Hashimoto [Japon] ; Michael Hertl [Allemagne] ; Nico Hunzelmann [Allemagne] ; Pilar Iranzo [Espagne] ; Pascal Joly [France] ; Marcel F. Jonkman [Pays-Bas] ; Yasuo Kitajima [Japon] ; Neil J. Korman [États-Unis] ; Linda K. Martin [Australie] ; Daniel Mimouni [Israël] ; Amit G. Pandya [États-Unis] ; Aimee S. Payne [États-Unis] ; David Rubenstein [États-Unis] ; Hiroshi Shimizu [Japon] ; Animesh A. Sinha [États-Unis] ; David Sirois [États-Unis] ; Detlef Zillikens ; Victoria P. Werth [États-Unis]

Source :

RBID : Pascal:08-0281029

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English descriptors

Abstract

Our scientific knowledge of pemphigus has dramatically progressed in recent years. However, despite the availability of various therapeutic options for the treatment of inflammatory diseases, only a few multicenter controlled trials have helped to define effective therapies in pemphigus. A major obstacle in comparing therapeutic outcomes between centers is the lack of generally accepted definitions and measurements for the clinical evaluation of patients with pemphigus. Common terms and end points of pemphigus are needed so that experts in the field can accurately measure and assess disease extent, activity, severity, and therapeutic response, and thus facilitate and advance clinical trials. This consensus statement from the International Pemphigus Committee represents 2 years of collaborative efforts to attain mutually acceptable common definitions for pemphigus. These should assist in development of consistent reporting of outcomes in future studies.

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Le document en format XML

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<title xml:lang="en" level="a">Consensus statement on definitions of disease, end points, and therapeutic response for pemphigus</title>
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<placeName>
<settlement type="city">Boston</settlement>
<region type="state">Massachusetts</region>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Amagai, Masayuki" sort="Amagai, Masayuki" uniqKey="Amagai M" first="Masayuki" last="Amagai">Masayuki Amagai</name>
<affiliation wicri:level="3">
<inist:fA14 i1="04">
<s1>Keio University School of Medicine</s1>
<s2>Tokyo</s2>
<s3>JPN</s3>
<sZ>4 aut.</sZ>
</inist:fA14>
<country>Japon</country>
<placeName>
<settlement type="city">Tokyo</settlement>
<region type="région">Région de Kantō</region>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Barnadas, Maria A" sort="Barnadas, Maria A" uniqKey="Barnadas M" first="Maria A." last="Barnadas">Maria A. Barnadas</name>
<affiliation wicri:level="3">
<inist:fA14 i1="05">
<s1>Hospital de la Santa Creu i Sant Pau</s1>
<s2>Barcelona</s2>
<s3>ESP</s3>
<sZ>5 aut.</sZ>
</inist:fA14>
<country>Espagne</country>
<placeName>
<settlement type="city">Barcelone</settlement>
<region nuts="2" type="region">Catalogne</region>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Borradori, Luca" sort="Borradori, Luca" uniqKey="Borradori L" first="Luca" last="Borradori">Luca Borradori</name>
<affiliation wicri:level="1">
<inist:fA14 i1="06">
<s1>Hôpital Cantonal Universitaire</s1>
<s2>Geneva</s2>
<s3>CHE</s3>
<sZ>6 aut.</sZ>
</inist:fA14>
<country>Suisse</country>
<wicri:noRegion>Hôpital Cantonal Universitaire</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Bystryn, Jean Claude" sort="Bystryn, Jean Claude" uniqKey="Bystryn J" first="Jean-Claude" last="Bystryn">Jean-Claude Bystryn</name>
<affiliation wicri:level="1">
<inist:fA14 i1="07">
<s1>New York University Medical Center</s1>
<s3>USA</s3>
<sZ>7 aut.</sZ>
</inist:fA14>
<country>États-Unis</country>
<wicri:noRegion>New York University Medical Center</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Cianchini, Giuseppe" sort="Cianchini, Giuseppe" uniqKey="Cianchini G" first="Giuseppe" last="Cianchini">Giuseppe Cianchini</name>
<affiliation wicri:level="3">
<inist:fA14 i1="08">
<s1>Immunodermatology Department, Istituto Dermopatico dell'lmmacolata, I.R.C.C.S., Via dei Monti di Creta</s1>
<s2>Rome</s2>
<s3>ITA</s3>
<sZ>8 aut.</sZ>
</inist:fA14>
<country>Italie</country>
<placeName>
<settlement type="city">Rome</settlement>
<region nuts="2">Latium</region>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Diaz, Luis" sort="Diaz, Luis" uniqKey="Diaz L" first="Luis" last="Diaz">Luis Diaz</name>
<affiliation wicri:level="1">
<inist:fA14 i1="09">
<s1>University of North Carolina</s1>
<s2>Chapel Hill</s2>
<s3>USA</s3>
<sZ>9 aut.</sZ>
<sZ>25 aut.</sZ>
</inist:fA14>
<country>États-Unis</country>
<wicri:noRegion>University of North Carolina</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Fivenson, David" sort="Fivenson, David" uniqKey="Fivenson D" first="David" last="Fivenson">David Fivenson</name>
<affiliation wicri:level="1">
<inist:fA14 i1="10">
<s1>Private Practice</s1>
<s2>Ann Arbor</s2>
<s3>USA</s3>
<sZ>10 aut.</sZ>
</inist:fA14>
<country>États-Unis</country>
<wicri:noRegion>Private Practice</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Hall, Russell" sort="Hall, Russell" uniqKey="Hall R" first="Russell" last="Hall">Russell Hall</name>
<affiliation wicri:level="1">
<inist:fA14 i1="11">
<s1>Division of Dermatology, Duke Medical Center</s1>
<s2>Durham</s2>
<s3>USA</s3>
<sZ>11 aut.</sZ>
</inist:fA14>
<country>États-Unis</country>
<wicri:noRegion>Durham</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Harman, Karen E" sort="Harman, Karen E" uniqKey="Harman K" first="Karen E." last="Harman">Karen E. Harman</name>
<affiliation wicri:level="1">
<inist:fA14 i1="12">
<s1>University Hospitals Leicester</s1>
<s3>GBR</s3>
<sZ>12 aut.</sZ>
</inist:fA14>
<country>Royaume-Uni</country>
<wicri:noRegion>University Hospitals Leicester</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Hashimoto, Takashi" sort="Hashimoto, Takashi" uniqKey="Hashimoto T" first="Takashi" last="Hashimoto">Takashi Hashimoto</name>
<affiliation wicri:level="1">
<inist:fA14 i1="13">
<s1>Kurume University School of Medicine</s1>
<s3>JPN</s3>
<sZ>13 aut.</sZ>
</inist:fA14>
<country>Japon</country>
<wicri:noRegion>Kurume University School of Medicine</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Hertl, Michael" sort="Hertl, Michael" uniqKey="Hertl M" first="Michael" last="Hertl">Michael Hertl</name>
<affiliation wicri:level="1">
<inist:fA14 i1="14">
<s1>Universitätsklinikum GieBen und Marburg GmbH</s1>
<s3>DEU</s3>
<sZ>14 aut.</sZ>
</inist:fA14>
<country>Allemagne</country>
<wicri:noRegion>Universitätsklinikum GieBen und Marburg GmbH</wicri:noRegion>
<wicri:noRegion>Universitätsklinikum GieBen und Marburg GmbH</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Hunzelmann, Nico" sort="Hunzelmann, Nico" uniqKey="Hunzelmann N" first="Nico" last="Hunzelmann">Nico Hunzelmann</name>
<affiliation wicri:level="1">
<inist:fA14 i1="15">
<s1>Universitätshautklinik Köln</s1>
<s3>DEU</s3>
<sZ>15 aut.</sZ>
</inist:fA14>
<country>Allemagne</country>
<wicri:noRegion>Universitätshautklinik Köln</wicri:noRegion>
<wicri:noRegion>Universitätshautklinik Köln</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Iranzo, Pilar" sort="Iranzo, Pilar" uniqKey="Iranzo P" first="Pilar" last="Iranzo">Pilar Iranzo</name>
<affiliation wicri:level="4">
<inist:fA14 i1="16">
<s1>Hospital Clínic, Universitat de Barcelona</s1>
<s3>ESP</s3>
<sZ>16 aut.</sZ>
</inist:fA14>
<country>Espagne</country>
<placeName>
<settlement type="city">Barcelone</settlement>
<region nuts="2" type="region">Catalogne</region>
</placeName>
<orgName type="university">Université de Barcelone</orgName>
</affiliation>
</author>
<author>
<name sortKey="Joly, Pascal" sort="Joly, Pascal" uniqKey="Joly P" first="Pascal" last="Joly">Pascal Joly</name>
<affiliation wicri:level="3">
<inist:fA14 i1="17">
<s1>Clinique Dermatologique, Hopital Charles Nicolle</s1>
<s2>Rouen</s2>
<s3>FRA</s3>
<sZ>17 aut.</sZ>
</inist:fA14>
<country>France</country>
<placeName>
<region type="region">Région Normandie</region>
<region type="old region">Haute-Normandie</region>
<settlement type="city">Rouen</settlement>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Jonkman, Marcel F" sort="Jonkman, Marcel F" uniqKey="Jonkman M" first="Marcel F." last="Jonkman">Marcel F. Jonkman</name>
<affiliation wicri:level="4">
<inist:fA14 i1="18">
<s1>University Medical Center Groningen, University of Groningen</s1>
<s3>NLD</s3>
<sZ>18 aut.</sZ>
</inist:fA14>
<country>Pays-Bas</country>
<placeName>
<settlement type="city">Groningue (ville)</settlement>
<region>Groningue (province)</region>
</placeName>
<orgName type="university">Université de Groningue</orgName>
</affiliation>
</author>
<author>
<name sortKey="Kitajima, Yasuo" sort="Kitajima, Yasuo" uniqKey="Kitajima Y" first="Yasuo" last="Kitajima">Yasuo Kitajima</name>
<affiliation wicri:level="1">
<inist:fA14 i1="19">
<s1>Gifu University School of Medicine</s1>
<s3>JPN</s3>
<sZ>19 aut.</sZ>
</inist:fA14>
<country>Japon</country>
<wicri:noRegion>Gifu University School of Medicine</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Korman, Neil J" sort="Korman, Neil J" uniqKey="Korman N" first="Neil J." last="Korman">Neil J. Korman</name>
<affiliation wicri:level="1">
<inist:fA14 i1="20">
<s1>University Hospitals Case Medical Center</s1>
<s2>Cleveland</s2>
<s3>USA</s3>
<sZ>20 aut.</sZ>
</inist:fA14>
<country>États-Unis</country>
<wicri:noRegion>University Hospitals Case Medical Center</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Martin, Linda K" sort="Martin, Linda K" uniqKey="Martin L" first="Linda K." last="Martin">Linda K. Martin</name>
<affiliation wicri:level="3">
<inist:fA14 i1="01">
<s1>Departments of Dermatology at St George Hospital, University of NSW</s1>
<s2>Sydney</s2>
<s3>AUS</s3>
<sZ>1 aut.</sZ>
<sZ>21 aut.</sZ>
</inist:fA14>
<country>Australie</country>
<placeName>
<settlement type="city">Sydney</settlement>
<region type="état">Nouvelle-Galles du Sud</region>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Mimouni, Daniel" sort="Mimouni, Daniel" uniqKey="Mimouni D" first="Daniel" last="Mimouni">Daniel Mimouni</name>
<affiliation wicri:level="1">
<inist:fA14 i1="21">
<s1>Rabin Medical Center</s1>
<s2>Petah-Tikva</s2>
<s3>ISR</s3>
<sZ>22 aut.</sZ>
</inist:fA14>
<country>Israël</country>
<wicri:noRegion>Rabin Medical Center</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Pandya, Amit G" sort="Pandya, Amit G" uniqKey="Pandya A" first="Amit G." last="Pandya">Amit G. Pandya</name>
<affiliation wicri:level="3">
<inist:fA14 i1="22">
<s1>University of Texas Southwestern Medical Center</s1>
<s2>Dallas</s2>
<s3>USA</s3>
<sZ>23 aut.</sZ>
</inist:fA14>
<country>États-Unis</country>
<placeName>
<settlement type="city">Dallas</settlement>
<region type="state">Texas</region>
</placeName>
</affiliation>
</author>
<author>
<name sortKey="Payne, Aimee S" sort="Payne, Aimee S" uniqKey="Payne A" first="Aimee S." last="Payne">Aimee S. Payne</name>
<affiliation wicri:level="1">
<inist:fA14 i1="02">
<s1>University of Pennsylvania</s1>
<s3>USA</s3>
<sZ>2 aut.</sZ>
<sZ>24 aut.</sZ>
<sZ>30 aut.</sZ>
</inist:fA14>
<country>États-Unis</country>
<wicri:noRegion>University of Pennsylvania</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Rubenstein, David" sort="Rubenstein, David" uniqKey="Rubenstein D" first="David" last="Rubenstein">David Rubenstein</name>
<affiliation wicri:level="1">
<inist:fA14 i1="09">
<s1>University of North Carolina</s1>
<s2>Chapel Hill</s2>
<s3>USA</s3>
<sZ>9 aut.</sZ>
<sZ>25 aut.</sZ>
</inist:fA14>
<country>États-Unis</country>
<wicri:noRegion>University of North Carolina</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Shimizu, Hiroshi" sort="Shimizu, Hiroshi" uniqKey="Shimizu H" first="Hiroshi" last="Shimizu">Hiroshi Shimizu</name>
<affiliation wicri:level="1">
<inist:fA14 i1="23">
<s1>Hokkaido University Graduate School of Medicine</s1>
<s2>Sapporo</s2>
<s3>JPN</s3>
<sZ>26 aut.</sZ>
</inist:fA14>
<country>Japon</country>
<wicri:noRegion>Hokkaido University Graduate School of Medicine</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Sinha, Animesh A" sort="Sinha, Animesh A" uniqKey="Sinha A" first="Animesh A." last="Sinha">Animesh A. Sinha</name>
<affiliation wicri:level="4">
<inist:fA14 i1="24">
<s1>Center for Investigative Dermatology, Division of Dermatology and Cutaneous Sciences, Michigan State University</s1>
<s2>East Lansing</s2>
<s3>USA</s3>
<sZ>27 aut.</sZ>
</inist:fA14>
<country>États-Unis</country>
<placeName>
<settlement type="city">East Lansing</settlement>
<region type="state">Michigan</region>
</placeName>
<orgName type="university">Université d'État du Michigan</orgName>
</affiliation>
</author>
<author>
<name sortKey="Sirois, David" sort="Sirois, David" uniqKey="Sirois D" first="David" last="Sirois">David Sirois</name>
<affiliation wicri:level="1">
<inist:fA14 i1="25">
<s1>Department of Oral Medicine, New York University College of Dentistry</s1>
<s3>USA</s3>
<sZ>28 aut.</sZ>
</inist:fA14>
<country>États-Unis</country>
<wicri:noRegion>Department of Oral Medicine, New York University College of Dentistry</wicri:noRegion>
</affiliation>
</author>
<author>
<name sortKey="Zillikens, Detlef" sort="Zillikens, Detlef" uniqKey="Zillikens D" first="Detlef" last="Zillikens">Detlef Zillikens</name>
</author>
<author>
<name sortKey="Werth, Victoria P" sort="Werth, Victoria P" uniqKey="Werth V" first="Victoria P." last="Werth">Victoria P. Werth</name>
<affiliation wicri:level="1">
<inist:fA14 i1="02">
<s1>University of Pennsylvania</s1>
<s3>USA</s3>
<sZ>2 aut.</sZ>
<sZ>24 aut.</sZ>
<sZ>30 aut.</sZ>
</inist:fA14>
<country>États-Unis</country>
<wicri:noRegion>University of Pennsylvania</wicri:noRegion>
</affiliation>
</author>
</analytic>
<series>
<title level="j" type="main">Journal of the American Academy of Dermatology</title>
<title level="j" type="abbreviated">J. Am. Acad. Dermatol.</title>
<idno type="ISSN">0190-9622</idno>
<imprint>
<date when="2008">2008</date>
</imprint>
</series>
</biblStruct>
</sourceDesc>
<seriesStmt>
<title level="j" type="main">Journal of the American Academy of Dermatology</title>
<title level="j" type="abbreviated">J. Am. Acad. Dermatol.</title>
<idno type="ISSN">0190-9622</idno>
</seriesStmt>
</fileDesc>
<profileDesc>
<textClass>
<keywords scheme="KwdEn" xml:lang="en">
<term>Definition</term>
<term>Dermatology</term>
<term>End</term>
<term>Pemphigus</term>
<term>Treatment</term>
</keywords>
<keywords scheme="Pascal" xml:lang="fr">
<term>Pemphigus</term>
<term>Définition</term>
<term>Extrémité</term>
<term>Traitement</term>
<term>Dermatologie</term>
</keywords>
</textClass>
</profileDesc>
</teiHeader>
<front>
<div type="abstract" xml:lang="en">Our scientific knowledge of pemphigus has dramatically progressed in recent years. However, despite the availability of various therapeutic options for the treatment of inflammatory diseases, only a few multicenter controlled trials have helped to define effective therapies in pemphigus. A major obstacle in comparing therapeutic outcomes between centers is the lack of generally accepted definitions and measurements for the clinical evaluation of patients with pemphigus. Common terms and end points of pemphigus are needed so that experts in the field can accurately measure and assess disease extent, activity, severity, and therapeutic response, and thus facilitate and advance clinical trials. This consensus statement from the International Pemphigus Committee represents 2 years of collaborative efforts to attain mutually acceptable common definitions for pemphigus. These should assist in development of consistent reporting of outcomes in future studies.</div>
</front>
</TEI>
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<li>Japon</li>
<li>Pays-Bas</li>
<li>Royaume-Uni</li>
<li>Suisse</li>
<li>États-Unis</li>
</country>
<region>
<li>Catalogne</li>
<li>Groningue (province)</li>
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<li>Rome</li>
<li>Rouen</li>
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<li>Tokyo</li>
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<li>Université d'État du Michigan</li>
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</list>
<tree>
<noCountry>
<name sortKey="Zillikens, Detlef" sort="Zillikens, Detlef" uniqKey="Zillikens D" first="Detlef" last="Zillikens">Detlef Zillikens</name>
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<region name="Nouvelle-Galles du Sud">
<name sortKey="Murrell, Dedee F" sort="Murrell, Dedee F" uniqKey="Murrell D" first="Dedee F." last="Murrell">Dedee F. Murrell</name>
</region>
<name sortKey="Martin, Linda K" sort="Martin, Linda K" uniqKey="Martin L" first="Linda K." last="Martin">Linda K. Martin</name>
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<name sortKey="Pandya, Amit G" sort="Pandya, Amit G" uniqKey="Pandya A" first="Amit G." last="Pandya">Amit G. Pandya</name>
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<name sortKey="Rubenstein, David" sort="Rubenstein, David" uniqKey="Rubenstein D" first="David" last="Rubenstein">David Rubenstein</name>
<name sortKey="Sinha, Animesh A" sort="Sinha, Animesh A" uniqKey="Sinha A" first="Animesh A." last="Sinha">Animesh A. Sinha</name>
<name sortKey="Sirois, David" sort="Sirois, David" uniqKey="Sirois D" first="David" last="Sirois">David Sirois</name>
<name sortKey="Werth, Victoria P" sort="Werth, Victoria P" uniqKey="Werth V" first="Victoria P." last="Werth">Victoria P. Werth</name>
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<name sortKey="Amagai, Masayuki" sort="Amagai, Masayuki" uniqKey="Amagai M" first="Masayuki" last="Amagai">Masayuki Amagai</name>
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<name sortKey="Hashimoto, Takashi" sort="Hashimoto, Takashi" uniqKey="Hashimoto T" first="Takashi" last="Hashimoto">Takashi Hashimoto</name>
<name sortKey="Kitajima, Yasuo" sort="Kitajima, Yasuo" uniqKey="Kitajima Y" first="Yasuo" last="Kitajima">Yasuo Kitajima</name>
<name sortKey="Shimizu, Hiroshi" sort="Shimizu, Hiroshi" uniqKey="Shimizu H" first="Hiroshi" last="Shimizu">Hiroshi Shimizu</name>
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<country name="Espagne">
<region name="Catalogne">
<name sortKey="Barnadas, Maria A" sort="Barnadas, Maria A" uniqKey="Barnadas M" first="Maria A." last="Barnadas">Maria A. Barnadas</name>
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<name sortKey="Borradori, Luca" sort="Borradori, Luca" uniqKey="Borradori L" first="Luca" last="Borradori">Luca Borradori</name>
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<country name="Italie">
<region name="Latium">
<name sortKey="Cianchini, Giuseppe" sort="Cianchini, Giuseppe" uniqKey="Cianchini G" first="Giuseppe" last="Cianchini">Giuseppe Cianchini</name>
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</country>
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<noRegion>
<name sortKey="Harman, Karen E" sort="Harman, Karen E" uniqKey="Harman K" first="Karen E." last="Harman">Karen E. Harman</name>
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<country name="Allemagne">
<noRegion>
<name sortKey="Hertl, Michael" sort="Hertl, Michael" uniqKey="Hertl M" first="Michael" last="Hertl">Michael Hertl</name>
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<name sortKey="Hunzelmann, Nico" sort="Hunzelmann, Nico" uniqKey="Hunzelmann N" first="Nico" last="Hunzelmann">Nico Hunzelmann</name>
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<country name="France">
<region name="Région Normandie">
<name sortKey="Joly, Pascal" sort="Joly, Pascal" uniqKey="Joly P" first="Pascal" last="Joly">Pascal Joly</name>
</region>
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<country name="Pays-Bas">
<region name="Groningue (province)">
<name sortKey="Jonkman, Marcel F" sort="Jonkman, Marcel F" uniqKey="Jonkman M" first="Marcel F." last="Jonkman">Marcel F. Jonkman</name>
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<country name="Israël">
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<name sortKey="Mimouni, Daniel" sort="Mimouni, Daniel" uniqKey="Mimouni D" first="Daniel" last="Mimouni">Daniel Mimouni</name>
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